Rare diseases -- Case studies : Unusual conditions that every orthopaedic surgeon should know : a case-based guide / Wilhelm A. Zuelzer, Sreenivasulu Metikala, editors
2024
1
4
Rare diseases -- Chemotherapy : Rare disease drug development : clinical, scientific, patient, and caregiver perspectives / Raymond A. Huml, editor
Rare diseases -- Genetic aspects : Genomics of rare diseases : understanding rare disease genetics / edited by Claudia Gonzaga-Jauregui and James R. Lupski
2021
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12
Rare Diseases -- genetics : Genetics of rare autoimmune diseases / Javier MartÃn, Francisco David Carmona, editors
2019
1
13
Rare Diseases -- pathology : Rare tumors in children and adolescents / Dominik T. Schneider [and others], editors
Rare diseases -- Treatment -- Research : Innovative designs and analyses for small population clinical trials : development strategies and operational engagement for pediatric and rare diseases / Jingjing Ye, Lei Nie